Gene Therapy for Sickle-Cell Diseases| a Drug Pipeline Analysis Report 2018| Technavio

Technavio has published a new report on the drug development pipeline for gene therapy for sickle-cell diseases, including a detailed study of the pipeline molecules. (Graphic: Business Wire)

LONDON--()--Technavio has announced their latest pipeline analysis report on gene therapy for sickle-cell diseases. The report includes a detailed analysis of the pipeline molecules under investigation within the defined data collection period for gene therapy for sickle-cell diseases.

This report by Technavio presents a detailed analysis of the market, including regulatory framework, drug development strategies, recruitment strategies, and key companies that are expected to play an essential role in the growth of the market in the future.

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Sickle-cell diseases: Market overview

Sickle-cell diseases are a group of blood disorders caused by an abnormality in the hemoglobin in red blood cells. Sickle-cell diseases are inherited from parents. The patients inherit on copy of mutated hemoglobin gene from each parent in the chromosome 11. The people with one abnormal copy of the hemoglobin gene are called carriers, and they do not show the traits of disease or develop the anemia. People with two copies of the hemoglobin gene are at high risk of developing the disease. The disease can be cured to a small extent by bone marrow cell transplantation. Sickle-cell anemia constitutes a major part of sickle-cell diseases (almost 80% of sickle-cell diseases). Sickle-cell diseases can lead to severe complications such as stroke, chronic pain, pulmonary hypertension, and osteomyelitis.

According to a senior market research analyst at Technavio, “Sickle-cell diseases are race and geography-specific indications. The disease is more common in the Sub-Saharan regions, India, and the Middle-Eastern countries compared with other parts of the world.”

Gene therapy for sickle-cell diseases: Segmentation analysis

This drug pipeline analysis report segments the sickle-cell diseases market based on therapies employed (monotherapy), RoA (intravenous), therapeutic modality (gene), targets (CD34, and β-globin), MoA (gene therapy), geographical segmentation (US and France) and recruitment status (active, not recruiting, not applicable, and recruiting). It provides an in-depth analysis of the prominent factors influencing the market, including drivers, opportunities, trends, and industry-specific challenges.

Based on MoA, around 80% of the molecules that are being investigated for the treatment of sickle-cell diseases are gene therapy.

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Some of the key topics covered in the report include:

Scope of the Report

Regulatory Framework

Drug Development Landscape

  • Drugs under development
  • Indications coverage

Drug Development Strategies

  • Therapies employed
  • RoA
  • Therapeutic modality
  • Geographical coverage

Recruitment Strategies

  • Recruitment status
  • Gender
  • Age

Key Companies

  • Type of players
  • Company overview

Discontinued or Dormant Molecules

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Technavio Research
Jesse Maida
Media & Marketing Executive
US: +1 844 364 1100
UK: +44 203 893 3200

Release Summary

Technavio has published a new report on the drug development pipeline for gene therapy for sickle-cell diseases.


Technavio Research
Jesse Maida
Media & Marketing Executive
US: +1 844 364 1100
UK: +44 203 893 3200