Niemann-Pick Disease | A Pipeline Analysis Report 2018 | Technavio

Technavio has published a new report on the drug development pipeline for Niemann-pick disease, including a detailed study of the pipeline molecules. (Graphic: Business Wire)

LONDON--()--Technavio has announced their latest pipeline analysis report on the Niemann-Pick disease market. The report includes a detailed analysis of the pipeline molecules under investigation within the defined data collection period to treat Niemann-Pick disease.

This report by Technavio presents a detailed analysis of the market, including regulatory framework, drug development strategies, recruitment strategies, and key companies that are expected to play an essential role in the growth of the market in the future.

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Niemann-Pick disease: Market overview

Niemann-Pick disease is a rare, inherited disease that affects the body’s ability to metabolize cholesterol and lipids within cells. Niemann-Pick disease can affect the brain, nerves, liver, spleen, bone marrow, and lungs (in severe cases). People with Niemann-Pick disease experience symptoms related to the progressive function loss of the nerves, the brain, and other organs.

According to a senior market research analyst at Technavio, “Niemann-Pick disease can occur at any age, but it mainly affects children. The disease has no known cure and is sometimes fatal. According to the US National Library of Medicines, Niemann-Pick disease type A and B are estimated to affect 1 in 250,000 individuals. Niemann-Pick disease type A occurs more frequently among individuals of Ashkenazi, an Eastern and Central European Jewish descent, than in the general population.”

Niemann-Pick disease: Segmentation analysis

This pipeline analysis report segments the Niemann-Pick disease market based on therapies employed (monotherapy), RoA (oral, intravenous, and intrathecal), therapeutic modality (small molecule, oligosaccharide, recombinant enzyme, and amino acid), targets (cholesterol, sphingomyelin, human ASM, PKC epsilon, HSP 70, and histone deacetylase), MoA (cholesterol modulator, sphingomyelin inhibitor, ASM replacement, PKC epsilon inhibitor, HSP 70 inducer, and HDAC inhibitor), geographical segmentation (US, UK, France, Italy, Germany, and others) and recruitment status (active, not recruiting, completed, recruiting, and enrolling by invitation). It provides an in-depth analysis of the prominent factors influencing the market, including drivers, opportunities, trends, and industry-specific challenges.

Based on therapeutic modality, around 42% of the molecules that are being investigated for the treatment of Niemann-Pick disease are small molecule.

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Some of the key topics covered in the report include:

Scope of the Report

Regulatory Framework

Drug Development Landscape

  • Drugs under development
  • Indications coverage

Drug Development Strategies

  • Therapies employed
  • RoA
  • Therapeutic modality
  • Geographical coverage

Recruitment Strategies

  • Recruitment status
  • Gender
  • Age

Key Companies

  • Type of players
  • Company overview

Discontinued or Dormant Molecules

About Technavio

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Technavio Research
Jesse Maida
Media & Marketing Executive
US: +1 844 364 1100
UK: +44 203 893 3200

Release Summary

Technavio has published a new report on the drug development pipeline for Niemann-pick disease, including a study of the pipeline molecules.


Technavio Research
Jesse Maida
Media & Marketing Executive
US: +1 844 364 1100
UK: +44 203 893 3200